Continuing nintedanib treatment could be beneficial even in patients with PPF and IPF who would not be included in studies ...

Italian researchers found that 62% of patients with early-stage Huntington disease (HD) lacked insight into their motor ...

The US Food and Drug Administration (FDA) has accepted a supplemental New Drug Application for nebulized treprostinil for the ...

The safety profile has generally been manageable, although cytopenias, gastrointestinal symptoms, and differentiation ...

Progressive pulmonary fibrosis (PPF) is undercoded and underrecognized, according to electronic health record evidence.

In a new study, nearly half of individuals with NF1 had cherry angiomas, suggesting a previously unrecognized link.

Analysis of a national registry of hospital data found racial gaps in blood transfusion rates among patients hospitalized for ...

A woman living with HAE recalls her worst swelling episode yet and how it has affected the way she views the good days.

Survey responses revealed a notable disconnect between how patients with PNH and their physicians perceive symptoms, ...

Younger patients with MDS had lower-risk disease features and significantly better overall and leukemia-free survival.

Comprehensive care is about assessing each patient’s needs and bringing the right professionals to the table. No two cases of ...

A woman with hypoplastic low-risk MDS had reversible cytopenic flares in 2 pregnancies, with blood counts returning to normal ...