Columnist Connie Chandler asked her caregivers what they think matters most to her, and many agreed it was all about the ...

Columnist Kevin Schaefer celebrates the approval of Isembyld for SMA, and remembers the relentless enthusiasm of his friend ...

Columnist Brianna Albers used to trust her doctors completely, but having a rare disease forced her to recognize they don't know everything.

The muscle-strengthening agent apitegromab, now Isembyld, has been approved in the U.S. as an add-on treatment for spinal muscular atrophy.

After going viral on social media, columnist Sherry Toh says her eyes were opened to how much people engage with content that ...

A European survey found that while treatment options have expanded, SMA patients still face limited access to medicines and ...

A new blood test detected 95% of homozygous SMN1 deletions, the cause of most SMA cases, with results available in about an ...

Advocates share key strategies for living with SMA to help patients successfully navigate careers, romance, and air travel.

Columnist Connie Chandler's relationship with her wheelchair is complicated, but she's learned it helps her tell her story ...

After months of struggling with tachycardia, guest writer Joanna Buoniconti says the episodes have become less frequent and ...

Cell machinery involved in histone production may take on new roles in mature nerve and muscle cells, offering clues about ...

I have a really special and pretty large friendship caregiving team, which I write about a lot in this column. Because I live with SMA, I need plenty of help, and I am grateful for all the wonderful ...